FDA grants “Investigational New Drug” status to Huntingtin-lowering gene-therapy agent AMT-130, clearing path to human trials in Huntington’s Disease patients
This fall sees exciting announcements from a number of companies focused on novel Huntingtin Lowering technologies, including Wave, PTC and Voyager
Media reports of a wonder drug for neurodegenerative diseases like Huntington's disease are overhyped
Work with genome editing techniques (zinc fingers and CRISPR) brings these tools closer to use in HD clinical trials
Major Announcement: First HD patients treated with gene silencing drugs
How will we know whether HD-lowering treatments are working? New advancements in the detection of mutant huntingtin.
Does a specific amino acid deficiency contribute to the development of HD?
A new study claims that high-dose creatine "slows the onset of Huntington Disease". How much hope and how much hype?
Prana Biotechnology has released data demonstrating their drug, PBT2, is effective in animal models of HD