Articles with the topic: gene-therapy

Advances on many fronts in the battle against the protein that causes Huntington's disease

Advances on many fronts in the battle against the protein that causes Huntington's disease

This fall sees exciting announcements from a number of companies focused on novel Huntingtin Lowering technologies, including Wave, PTC and Voyager

Dr Jeff CarrollDecember 04, 2018

New roles for huntingtin: removing a healthy protein to understand its function

New roles for huntingtin: removing a healthy protein to understand its function

Completely removing normal huntingtin in adults may disrupt healthy brain function, a recent study suggests.

Dr Leora FoxSeptember 26, 2017

Important advances in next generation genome editing tools for Huntington's Disease

Important advances in next generation genome editing tools for Huntington's Disease

Work with genome editing techniques (zinc fingers and CRISPR) brings these tools closer to use in HD clinical trials

Mr. Shawn MinnigOctober 31, 2016

Could a new "jaw-dropping" breakthrough help treat Huntington's Disease?

Could a new "jaw-dropping" breakthrough help treat Huntington's Disease?

The news has recently been full of stories about CRISPR, a new "jaw-dropping" DNA-editing technology. Hype or hope?

Dr Jeff CarrollFebruary 25, 2016

Giving Huntington's disease the finger? Two teams report success for zinc-finger drugs in cells and mice

Giving Huntington's disease the finger? Two teams report success for zinc-finger drugs in cells and mice

Success in Huntington’s disease cells and mice for zinc finger drugs that reduce production of the harmful protein

Professor Ed WildNovember 01, 2012

Gene therapy meets stem cells in liver disease success

Gene therapy meets stem cells in liver disease success

Scientists combine gene therapy and stem cells to correct a genetic liver disease. Could this combo be retooled for H

Dr Michael OrthDecember 26, 2011

Ten golden rules for reading a scientific news story

Ten golden rules for reading a scientific news story

Avoid the hype: HDBuzz presents ten 'golden rules' for reading a news story or press release about Huntington's disea

Professor Ed WildSeptember 05, 2011

Cut-and-paste DNA: fixing mutations with 'genome editing'

Cut-and-paste DNA: fixing mutations with 'genome editing'

Scientists make precise changes to the DNA of a live animal. Could it work for human genetic diseases?

Dr Jeff CarrollJuly 18, 2011