A new system has been developed that allows researchers to fine-tune gene expression with oral drugs, work that provides a powerful tool for gene editing.
A new study by researchers at Johns Hopkins describes a non-invasive way to track progression of Huntington’s disease. This could be used before patients even start showing symptoms to help test treatments in early stages of disease.
A successful early trial of a drug for Familial Transthyretic Amyloidosis showed that CRISPR gene editing could be safely used in the human body. What does this mean for gene editing in HD?
A recent series of studies on the gene-editing method CRISPR have raised concerns about the suitability of this technology for the treatment of genetic illnesses such as Huntington's disease
Scientists screen the ENTIRE genome to find new potential therapeutic targets for HD. This ambitious study provides a wealth of data for HD researchers
For the first time in HD research, an animal model has been created in pigs using 2 cutting edge DNA editing t
A surprising new paper sheds light on the role of the HD gene early in development. Should we worry?
CRISPR genome editing just got an off-switch. We cut through the hype to explore the technology in HD
Evolving CRISPR-Cas9 techniques can now be used to edit the HD gene in a living mouse brain.