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'Floating' gene-silencing drugs into the brain with exosomes

'Floating' gene-silencing drugs into the brain with exosomes

Exosomes – tiny bubbles made by cells – could be used to get gene silencing drugs from the bloodstream into the brain

Professor Ed WildMay 19, 2011

Gene silencing takes a targeted step forward

Gene silencing takes a targeted step forward

Targeting the mutant Huntington's disease gene for silencing, while leaving the healthy gene untouched

Dr Michael OrthOctober 07, 2011

Safety trials add crucial piece to gene silencing jigsaw

Safety trials add crucial piece to gene silencing jigsaw

Three trials of drugs to 'silence' the HD gene in monkeys show they hit the target safely. Human trials coming soon.

Professor Ed WildNovember 14, 2011

Double success for huntingtin RNAi gene silencing

Double success for huntingtin RNAi gene silencing

2 bits of good news for RNAi gene silencing in HD: it's safe over six months, and a way to treat bigger brain areas

Professor Ed WildJanuary 24, 2012

Could mesenchymal stem cells deliver gene silencing drugs?

Could mesenchymal stem cells deliver gene silencing drugs?

Stem cells can deliver HD gene silencing drugs into cells in a dish. Do we need another delivery technology?

Dr Jeff CarrollJanuary 31, 2012

ASO gene silencing reaches further, lasts longer

ASO gene silencing reaches further, lasts longer

Silencing the Huntingtin gene using ASO drugs reaches further, lasts longer and is safe. Human trial soon?

Dr Nayana LahiriJune 21, 2012

Shooting the messenger with single-stranded RNA gene silencing

Shooting the messenger with single-stranded RNA gene silencing

New ‘single-stranded RNA’ gene silencing drugs could be safer & more effective to treat Huntington’s disease

Dr Nayana LahiriSeptember 24, 2012

Major Roche-Isis deal boosts Huntington's disease gene silencing

Major Roche-Isis deal boosts Huntington's disease gene silencing

'ASO' gene silencing drugs for HD boosted by major deal between Isis Pharmaceuticals and Roche

Professor Ed WildApril 09, 2013

Gene silencing drug safe in ALS patients... bring on Huntington's disease trials

Gene silencing drug safe in ALS patients... bring on Huntington's disease trials

Gene silencing drug injected into spinal fluid in ALS patients proves safe. Good news for similar planned HD trials.

Joseph OchabaJune 29, 2013

Liftoff: First humans treated with gene silencing drugs for HD!

Liftoff: First humans treated with gene silencing drugs for HD!

Major Announcement: First HD patients treated with gene silencing drugs

Dr Jeff CarrollOctober 22, 2015

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