A new system has been developed that allows researchers to fine-tune gene expression with oral drugs, work that provides a powerful tool for gene editing.
A successful early trial of a drug for Familial Transthyretic Amyloidosis showed that CRISPR gene editing could be safely used in the human body. What does this mean for gene editing in HD?
A recent series of studies on the gene-editing method CRISPR have raised concerns about the suitability of this technology for the treatment of genetic illnesses such as Huntington's disease
A collaborative team of scientists from Canada and Japan have identified a small molecule which can change the CAG-repeat length in different lab models of Huntington's disease. #HuntingtonsDisease #DrugDiscovery
Scientists screen the ENTIRE genome to find new potential therapeutic targets for HD. This ambitious study provides a wealth of data for HD researchers
For the first time in HD research, an animal model has been created in pigs using 2 cutting edge DNA editing t
A surprising new paper sheds light on the role of the HD gene early in development. Should we worry?
CRISPR genome editing just got an off-switch. We cut through the hype to explore the technology in HD
Evolving CRISPR-Cas9 techniques can now be used to edit the HD gene in a living mouse brain.