Hot off the presses - New publication gives more details about the results of Ionis and Roche's safety study with a Huntingtin-lowering ASO
This fall sees exciting announcements from a number of companies focused on novel Huntingtin Lowering technologies, including Wave, PTC and Voyager
Finally, a big study that shows what childhood HD looks like. This will help us work out if new drugs work in children too
Work with genome editing techniques (zinc fingers and CRISPR) brings these tools closer to use in HD clinical trials
A confusing story about a huntingtin lowering trial is published in the Telegraph, but cool new stuff is happening!
Major Announcement: First HD patients treated with gene silencing drugs
A better tool for HD trials! New research shows innovative way to measure mutant Huntingtin outside the brain
A clinical trial for an exciting therapy against HD is planned for 2015. The first step is to make sure it is safe.
Roche's 'brain shuttle' sneaks drugs past the blood-brain barrier. Could it work for HD gene silencing drugs?