gene-silencing
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Huntington's Disease Therapeutics Conference 2016 – day 2
7 min read
Strategies for getting rid of mutant huntingtin & clinical trial updates: day 2 of the HD therapeutics conference
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Harnessing the power of viruses to treat Huntington's disease
7 min read
Researchers design a virus to more effectively deliver gene-silencing drugs throughout the brain.
By Dr Leora Fox -
Liftoff: First humans treated with gene silencing drugs for HD!
8 min read
Major Announcement: First HD patients treated with gene silencing drugs
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New tool to measure outcomes in Huntington’s Disease clinical trials
6 min read
A better tool for HD trials! New research shows innovative way to measure mutant Huntingtin outside the brain
By Megan Krench -
Measuring harmful huntingtin protein in the brain’s bath water
4 min read
How will we know whether HD-lowering treatments are working? New advancements in the detection of mutant huntingtin.
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2015 Huntington's Disease Therapeutics Conference: Day 2
8 min read
Day 2 of updates from the annual HD Therapeutics Conference in Palm Springs
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Huntington's disease clinical trial announcement: huntingtin-lowering drug to enter Phase I trial in 2015
7 min read
A clinical trial for an exciting therapy against HD is planned for 2015. The first step is to make sure it is safe.
By Dr Leora Fox -
Could a 'brain shuttle' get Huntington's disease drugs to where they're needed?
5 min read
Roche's 'brain shuttle' sneaks drugs past the blood-brain barrier. Could it work for HD gene silencing drugs?
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'Buzzilia' from the Huntington's Disease World Congress: day 4
7 min read
#Buzzilia, day 4: Jeff and Ed's roundup of happenings from the closing day of the HD World Congress in Rio de Janeiro
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Gene silencing drug safe in ALS patients… bring on Huntington's disease trials
7 min read
Gene silencing drug injected into spinal fluid in ALS patients proves safe. Good news for similar planned HD trials.