New ‘single-stranded RNA’ gene silencing drugs could be safer & more effective to treat Huntington’s disease
Lithium gets a second chance in HD - with a new chemical delivery method, tested in Huntington’s disease mice
CHDI and Pfizer announce exciting animal work and plans for a human trial with a drug targeting 'phosphodiesterases'.
Exosomes – tiny bubbles made by cells – could be used to get gene silencing drugs from the bloodstream into the brain
Advanced drug screening techniques help scientists to make drugs that increase cellular recycling in neurons.