gene-therapy – Page 3

New roles for huntingtin: removing a healthy protein to understand its function

Completely removing normal huntingtin in adults may disrupt healthy brain function, a recent study suggests.

September 22, 2017

Work with genome editing techniques (zinc fingers and CRISPR) brings these tools closer to use in HD clinical trials

October 31, 2016

The news has recently been full of stories about CRISPR, a new "jaw-dropping" DNA-editing technology. Hype or hope?

November 13, 2013

Success in Huntington’s disease cells and mice for zinc finger drugs that reduce production of the harmful protein

November 1, 2012

Scientists combine gene therapy and stem cells to correct a genetic liver disease. Could this combo be retooled for H

December 26, 2011

Avoid the hype: HDBuzz presents ten 'golden rules' for reading a news story or press release about Huntington's disea

September 5, 2011

Scientists make precise changes to the DNA of a live animal. Could it work for human genetic diseases?

July 18, 2011